The BBC's Ben Morris describes living with spinal musclar atrophy, after Little Mix's Jessy Nelson spoke about it.

Former Little Mix star Jesy Nelson revealed on social media that her twin girls have been diagnosed with a rare genetic ...

Spinal muscular atrophy is a genetically inherited disorder that causes muscle weakness. Adults can get spinal muscular atrophy, but it’s rare in adults and progresses slowly. It doesn’t typically ...

Little Mix alum Jesy Nelson opened up in an emotional video Jan. 4 about her twin daughters’ Spinal Muscular Atrophy Type 1 diagnosis, a life-threatening disease that leads to severe muscle weakness.

For those of you that don't know what SMA 1 is, it is the most severe muscular disease that a baby can get," Jesy Nelson said ...

A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

Alice Wong, a disability rights activist with spinal muscular atrophy who died in November, left behind a legacy of advocacy ...

Spinal muscular atrophy (SMA) type 1 is a genetic condition in which the nerves that control movement, breathing, and swallowing become progressively weaker and smaller. SMA has five types with ...

A 5-year-old boy who was born with a rare genetic condition is now able to walk by himself, his mother has said, after ...

Injections for spinal muscular atrophy (SMA) refer to two treatments that the Food and Drug Administration (FDA) has approved for SMA: nusinersen (Spinraza) and onasemnogene abeparovec-xioi (Zolgensma ...