The Muscular Dystrophy Association (MDA) celebrates today's announcement that the U.S. Food and Drug Administration (FDA) has approved a High Dose Regimen of SPINRAZA(R) (nusinersen) for the treatment ...

"Managing pain in patients with SMA begins with the recognition that there are predictable etiologies leading to pain in SMA and investigating them during each medical visit is important to implement ...

Jesy Nelson’s twins were diagnosed with spinal muscular atrophy (SMA) too late but now the NHS will start testing babies at ...

Scholar Rock (NASDAQ:SRRK) shares climbed about 12% on Tuesday after the company announced it had resubmitted its Biologics ...

Biogen Inc. BIIB shares are up on Monday following the FDA’s approval of a new high-dose regimen for Spinraza (nusinersen), a ...

This high dose nusinersen regimen for spinal muscular atrophy includes 50mg loading doses and 28mg maintenance doses.

Campaigners hope pilot will result in heel prick test for rare condition being approved across Britain ...

The risk of scoliosis was largely related to what type of SMA a patient had, with those with type III having the lowest risk and those with type II developing scoliosis at a later age than those with ...

Panelists discuss how the current spinal muscular atrophy (SMA) treatment landscape includes 3 options: gene therapy (onasemnogene abeparvovec [Zolgensma]) for younger patients and 2 splice modifiers ...

Jesy Nelson has heralded an ‘amazing’ day as newborns to be tested by NHS for spinal muscular atrophy (SMA) - but adds: ‘I ...

Scotland is now screening every newborn for a condition that can kill within two years. Here is what parents across the UK need to know.

DUBLIN--(BUSINESS WIRE)--The "Spinal Muscular Atrophy (SMA) Treatment Market Size, Share & Trends Analysis Report By Route of Administration (Oral, Intrathecal), By Treatment (Gene Therapy, Drug), By ...